nusinersen | Ligand page | IUPHAR/BPS Guide to PHARMACOLOGY
Medicina | Free Full-Text | The Safety and Efficacy of Nusinersen in the Treatment of Spinal Muscular Atrophy: A Systematic Review and Meta-Analysis of Randomized Controlled Trials
Biomolecules | Free Full-Text | Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy
Spinraza (Nusinersen) for SMA | SMA News Today
IJMS | Free Full-Text | Nusinersen Modulates Proteomics Profiles of Cerebrospinal Fluid in Spinal Muscular Atrophy Type 1 Patients
CSF and plasma concentrations of nusinersen | Download Scientific Diagram
Advances in oligonucleotide drug delivery | Nature Reviews Drug Discovery
Discovery of a CNS penetrant small molecule SMN2 splicing modulator with improved tolerability for spinal muscular atrophy | Scientific Reports
Targeting the 5′ untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy: Molecular Therapy - Nucleic Acids
Nusinersen - Wikipedia
Quality of Life in SMA Patients Under Treatment With Nusinersen
Mechanism of action of nusinersen | Download Scientific Diagram
Nusinersen - an overview | ScienceDirect Topics
IJMS | Free Full-Text | High Concentration of an ISS-N1-Targeting Antisense Oligonucleotide Causes Massive Perturbation of the Transcriptome
How the discovery of ISS-N1 led to the first medical therapy for spinal muscular atrophy | Gene Therapy
Nusinersen (Spinraza®) – Spinal Muscular Atrophy (SMA) | National Institute of Neurological Disorders and Stroke
Spinraza, INN - nusinersen
FN170919 | 1258984-36-9 | Nusinersen | Biosynth
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study - The Lancet
Summary of Nusinersen Clinical Trials | Download Scientific Diagram
Biomolecules | Free Full-Text | Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy
Nusinersen - Wikipedia
Nusinersen - Wikipedia
